GalNAc-L96:高效RNA靶向递送的关键分子 ...
RNAi therapeutics have shown great success with multiple US Food and Drug Administration (FDA)-approved products involving N-acetyl galactosamine (GalNAc)-conjugated siRNAs to treat liver-targeted ...
为解决肝癌治疗难题,复旦大学附属肿瘤医院的研究人员开展 FAM99B 相关研究。发现 FAM99B 可抑制核糖体生成和肝癌进展,GalNAc - FAM99B65 - 146 有治疗潜力。该研究为肝癌治疗提供新思路,值得科研人员阅读。 复旦大学附属肿瘤医院(Fudan University Shanghai Cancer Center ...
Dosing underway in INLIGHT trial of WVE-007 in obesity with clinical data expected in 2H 2025; enrollment complete in first ...