A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

JP Morgan sees steady growth for Apellis' Syfovre, lowering the price target to $45. Syfovre sales hit $167.8M in Q4, with ...

Scholar Rock will present new Phase 3 SAPPHIRE trial data on apitegromab at the 2025 MDA conference, highlighting efficacy ...

Known as young onset dementia, when diagnosed in people under 65, this form of dementia can manifest in different ways than ...

Chinese AI agent Manus has shown how super intelligence can slowly take over human tasks. Like frogs in boiling water, we ...

A study based on a survey of 50 adults linked poorer quality sleep with more depressive symptoms and respiratory issues in ...

Spinal muscular atrophy type 1 is a genetic disorder that typically appears within the first six months of life, causing ...

Spinal Muscular Atrophy (SMA) is a genetic and hereditary disease characterized by a loss of muscle strength due to the ...

Multiple system atrophy (MSA) is not exactly a household word – a situation that Alterity Therapeutics is seeking to change.

Spinal bulbar muscular atrophy (SBMA) causes a loss of motor neurons in the spinal cord and brainstem. It mainly affects facial and swallowing muscles and the muscles in the arms and legs.

The General Insurance earned an overall score of 7.9 out of 10 thanks to its scores in coverage, cost, availability, reputation and customer experience. Discover if you are overpaying for car ...

cThe Dubowitz Neuromuscular Unit, UCL Great Ormond Street Institute of Child Health, NIHR Great Ormond Street Hospital Biomedical Research Centre and Great Ormond Street Hospital NHS Foundation Trust, ...