Patients with myotonic dystrophy face unique challenges in managing their ... 1-2 Recent studies presented at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference shed ...

Posters presented at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference show that therapeutic ...

Colton Belluzzo was diagnosed with a form of muscular dystrophy when he was a baby. The disease has weakened his muscles over time. But he and his family now have good reason to be optimistic.

WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.

The study uncovers the molecular 'rules' driving the arrangement of emerin into nanoclusters and the mechanisms leading to their defective assembly in people with muscular dystrophy. A new ...

FSHD is the second most common form of muscular dystrophy after the Duchenne type ... It tends to cause muscle wasting in the face, shoulder blades, and upper arms. The deal – which includes ...

Columnist Shalom Lim is sad to say goodbye to his caregiver of 18 years, but looks forward to the new chapter of life this ...

She said: “The fact that some parents want to separate their children who have muscular dystrophy and other rare diseases from society is just a minor challenge they face. They also need basic ...