In an interview, Scholar Rock's chief medical officer talks about benefits seen in clinical trials of its muscle-targeted SMA ...

Apitegromab, a fully human monoclonal antibody, works by selectively binding to the pro- and latent forms of myostatin in order to inhibit myostatin activation.

NASA Astronaut Sunita Williams has returned to Earth after spending over 9 moths in space - under microgravity. Even though she is back, her body is yet to re-adjust to gravity. But there is another ...

A Prescription Drug User Fee Act (PDUFA) target action date for apitegromab has been set for Sept. 22, 2025.

Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...

NASA astronaut Sunita Williams recently returned from space and is dealing with several health concerns. After spending ...

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

A leading fitness expert reveals four common walking mistakes that contribute to poor posture, joint pain, limited mobility ...

Space travel is risky for humans, but are AI robots ready to take over? Discover the challenges, potential, and future of ...

For patients who feel their Botox wears off quickly, Dr. Zalka often suggests increasing the dosage slightly. “Injecting a ...

Charcot-Marie-Tooth disease type 2E (CMT2E) is a slow and progressive neuropathy characterized by axonal dysfunction. Its clinical phenotype includes muscle weakness and atrophy, sensory loss and ...