Nanoscope Therapeutics is on the brink of filing for FDA approval of what could be the first gene therapy for incurable eye disease retinitis pigmentosa (RP) that can be used regardless of ...

The FDA has approved Krystal Biotech’s gene therapy Vyjuvek for dystrophic epidermolysis bullosa (DEB), a rare genetic disease characterised by fragile skin that can split and blister even with ...

Using gene editing with CRISPR-Cas9, the team has been able to study these proteins without altering ... Dec. 13, 2024 — Microorganisms produce a wide variety of natural products that can be ...

B-cell acute lymphoblastic leukemia (B-ALL) is a life-threatening and highly aggressive form of blood cancer. It is the most ...

The Secret History of America’s Role in the Ukraine War Part 1 Building Trust — and a Killing Machine Part 2 ‘When You Defeat Russia, We Will Make You Blue for Good’ Part 3 The Best-Laid ...

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which Leerink Partners’ Joseph Schwartz noted was greater than Sarepta Therapeutics showed with its Elevidys gene therapy, which the FDA approved in 2023. But perhaps more notably, Wave touted ...

HAYWARD, Calif., March 25, 2025 (GLOBE NEWSWIRE) -- Benitec Biopharma Inc. (Nasdaq: BNTC) ("Benitec” or the "Company”), a clinical-stage, gene therapy-focused, biotechnology company developing novel ...

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