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蔡宇伽/洪佳旭团队开发基于病毒样颗粒的新型基因编辑递送工具,为 ...
研究团队表示,RIDE 系统的成功开发为亨廷顿舞蹈症的治疗带来了新希望,并有望在未来应用于其他神经退行性疾病和遗传性疾病的治疗。随着进一步的研究和临床试验,RIDE 有望成为基因编辑领域的重要工具,助力基因治疗的发展和普及。
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